Gene Therapy Mitochondrial Disorders Cancer Gene Editing Muscular Dystrophy Lissencephaly Neurodegenerative Diseases Acute Myeloid Leukemia Research Studies Clinical Trials Hearing Loss ALS Disease Risk Assessment Aging Duchenne Muscular Dystrophy Cystic Fibrosis Muscular Dystrophies Mitochondrial Diseases Drug Targets Hemophilia B Cancer Research Neurological Disorders Diagnosis
Backed by a £10 million Wellcome Trust grant, the project will build human DNA strands in vitro through a parallel programme that addresses ethical and societal concerns.