Health ❯ Medical Research ❯ Genetic Disorders

Cystic Fibrosis

Hemophilia Treatment Development Gene Therapy

Researchers Debut Three Precision Gene Editing Tools Reducing Damage and Off-Target Errors

Each method leverages cellular mechanisms to curb errors.

2025 Lasker-DeBakey Award Honors Scientists Behind Trikafta’s Cystic Fibrosis Breakthrough