Health ❯ Medical Research ❯ Genetic Disorders

Gene Therapy

Cystic Fibrosis CRISPR Technology CPS1 Deficiency Gene Expression Control Precision Medicine

Researchers Debut Three Precision Gene Editing Tools Reducing Damage and Off-Target Errors

Each method leverages cellular mechanisms to curb errors.

Scientists Uncover Genetic ‘Dimmer Switch’ That Tunes Embryonic Gene Expression

Personalized CRISPR Therapy Sends Baby KJ Home from CHOP