Health ❯Medical Research

Gene Therapy

Ophthalmology Personalized Medicine Quality Control CRISPR Applications RNA Interference CRISPR Technology Inherited Conditions Viral Vectors siRNA Therapy MicroRNA Applications mRNA Technology Gene Manipulation MicroRNA Treatments Targeted Therapy Adeno-Associated Virus (AAV) mRNA Vaccines AFM-Téléthon Sickle Cell Disease Heart Failure Cardiovascular Health Epigenetic Editing Duchenne Muscular Dystrophy OTOF Gene OTOF Gene Therapy Hearing Restoration AAV Vectors Clinical Trials

Gene Therapy Reverses Heart Failure in Groundbreaking Animal Study

Researchers at the University of Utah report unprecedented recovery of heart function in pigs, paving the way for potential human trials in 2025.

Engineers Develop Faster, Safer Lipid Nanoparticles for mRNA Therapies

AI-Engineered DNA Switches Enable Precise Gene Control in Specific Cells

Innovative Nanoparticles Enhance Precision in mRNA and siRNA Therapies

New Genetic Tool Shows Promise in Treating High Cholesterol

Breakthrough Gene Therapies Offer New Hope for Sickle Cell Disease

Gene Therapy Shows Promise in Restoring Vision for Patients with Rare Genetic Disorder

Gene Therapy Shows Dramatic Vision Restoration in Rare Eye Condition

Gene Therapy Restores Hearing in Children with Hereditary Deafness

Gene Therapy Successfully Restores Hearing in Children with Hereditary Deafness