Health ❯Healthcare ❯Medical Research

Gene Therapy

Genetic Disorders Newborn Health Ophthalmology Innovations in Medicine Pediatric Care Medical Research Treatment Methods Vision Disorders Medical Treatments Patient Care

CRISPR Technique Reawakens Dormant Genes to Treat Blood Disorders

Early tests in human blood stem cells demonstrate the method’s potential to restore hemoglobin production with fewer risks than existing therapies

Study uncovers early-life window for in vivo gene therapy of blood stem cells

Penn Researchers Develop Gene Therapy Tools for Advanced Retinal Degenerations

Gene Therapy Restores Immune Function in Children with Rare Disorder