Healthcare ❯ Medical Treatments

Gene Therapy

CRISPR Technology Zolgensma Genetic Disorders Medical Innovations Patient Care Cost of Treatment Clinical Trials Neuromuscular Disorders CRISPR CAR T-cell Therapy

Personalized CRISPR Therapy Sends Baby KJ Home from CHOP

FDA fast-tracked the six-month custom CRISPR therapy that corrected KJ’s CPS1 mutation, enabling normal protein metabolism with reduced drug support.