Gene Therapy

Hearing Restoration CRISPR Applications In Vivo Editing Genome Editing Technologies CRISPR Systems Adeno-Associated Virus Regulatory Pathways CRISPR Technology Clinical Trials Ex Vivo Therapies

3 ARTICLES

last wk.

Lilly Acquires Engage Biologics for Up to $202 Million

The deal gives Lilly a preclinical Tethosome non‑viral DNA delivery platform, a lipid‑nanoparticle approach designed to target potency, tolerability and re‑dosing limits in DNA therapies.

3 ARTICLES

4mo ago

Aurora Therapeutics Launches to Scale Bespoke Gene Editing for PKU

7 ARTICLES

6mo ago

Prime Editing Tool PERT Debuts as Broad, One-Time Strategy for Nonsense Mutations

3 ARTICLES

7mo ago

Gene Therapy Restores Hearing in Children with Hereditary Deafness

Gene Therapy

Lilly Acquires Engage Biologics for Up to $202 Million

Aurora Therapeutics Launches to Scale Bespoke Gene Editing for PKU

Prime Editing Tool PERT Debuts as Broad, One-Time Strategy for Nonsense Mutations

Helex Raises $3.5 Million to Advance Kidney-Targeted Gene Therapies

Gene Therapy Shows 75% Slower Huntington’s Decline in Early Trial

mRNA-Style Antiviral Mimics Rare Mutation to Block Viruses for Days in Rodents

Scientists Decode Molecular Controls of the Hair Growth Cycle

Eight Healthy Babies Born Through UK Three-Parent IVF, Study Shows

Eli Lilly to Acquire Verve Therapeutics for $1.3 Billion

Scientists Use mRNA to Expose Hidden HIV in White Blood Cells

MIT Scientists Convert Skin Cells Directly Into Motor Neurons

Scientists Debate Safety and Ethics of Embryo Genome Editing to Prevent Disease

Gene Therapy Restores Hearing in Children with Hereditary Deafness