Health ❯ Medicine ❯ Genetics

Gene Therapy

OTOF Gene AAV-based Therapies CRISPR Technology GBA1 Hearing Loss Cyclin A2

Reactivated Fetal Gene Triggers Division of Adult Human Heart Cells in Lab

The Mount Sinai team will pursue safety testing ahead of an FDA application for early human trials.

Ambroxol Demonstrates Safety and Neuroprotection Signals in Parkinson’s Dementia Trial