Health ❯Medicine

Genetic Medicine

CRISPR-based Medicine Gene Therapies Gene Editing Gene Therapy Inherited Diseases

Precision Base Editor Restores Mitochondrial DNA in Patient Cells

It employs an mRNA-based DdCBE editor packaged in lipid nanoparticles to correct cytosine-to-thymine mutations inside mitochondria

FDA Approves Vertex/CRISPR Gene Therapy for Beta Thalassemia

FDA Approves First Gene Therapies for Sickle Cell Anemia