Science ❯Biotechnology ❯Genetic Engineering
Gene Editing Applications Gene Modification CRISPR-Cas System Therapeutic Applications Xenotransplantation Research Gene Editing in Transplants Transplantation Innovations Clinical Trials Gene Editing Patent Disputes Gene Therapy Clinical Applications Next-Generation Models
A groundbreaking treatment for CPS1 deficiency demonstrates the potential of tailored gene-editing therapies for rare diseases, with early results showing promising improvements.