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Clinical Trials

Cancer Vaccines Drug Development Research Funding Vaccine Trials Focused Ultrasound Gene Therapy Fetal Medicine

Postnatal Window Unlocks In Vivo Gene Therapy for Blood Stem Cells

Systemic lentiviral injection shortly after birth produced durable correction in mouse models, providing evidence of feasibility in human infants.

Philadelphia Doctors Pioneer Personalized Gene Therapy for Rare Metabolic Disorder

UCSF Research Advances Prenatal Therapy for Spinal Muscular Atrophy

UK Begins World-First Human Trial for Fridge-Free Vaccine