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Gene Therapy

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Aurora Therapeutics Launches to Scale Bespoke Gene Editing for PKU

Co-founded by Jennifer Doudna with Fyodor Urnov, the startup plans to use a base-editing platform under the FDA’s “plausible mechanism” pathway.

Prime Editing Tool PERT Debuts as Broad, One-Time Strategy for Nonsense Mutations

Gene Therapy Shows 75% Slower Huntington’s Decline in Early Trial

mRNA-Style Antiviral Mimics Rare Mutation to Block Viruses for Days in Rodents

Eli Lilly to Acquire Verve Therapeutics for $1.3 Billion