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Gene Therapy

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Sarepta Reports Early siRNA Data Showing Muscle Delivery as Shares Surge

The results suggest a working muscle delivery platform that could revive Sarepta’s pipeline.

UK Trial’s Base-Edited Off-the-Shelf CAR T Cells Deliver Durable Remissions in T-Cell Leukemia

Vinay Prasad Resigns as FDA Biologics Director After Politicized Tenure