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Drug Development Duchenne Muscular Dystrophy Autoimmune Diseases Cancer Treatment Immunotherapy Cancer Therapy Frontotemporal Dementia Antisense Oligonucleotides Rare Diseases Metabolic Diseases AI in Medicine Pulmonary Sarcoidosis Drug Efficacy Pediatric Medicine Alzheimer's Disease Nanobodies Phase 1 Studies Macrophage Therapy Eosinophilic Esophagitis Obesity Treatments Cancer Research Gene Therapy