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Duchenne Muscular Dystrophy

Sarepta Defies FDA Order to Halt Elevidys After Third Patient Death

The FDA paused clinical trials after three liver-failure deaths linked to the Duchenne gene therapy.

Sarepta Halts Elevidys Shipments for Non-Ambulatory Patients After Second Fatal Liver Failure

First Death Reported from Sarepta's Duchenne Gene Therapy Raises Safety Concerns