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Gene Therapy

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Lilly to Buy Adverum in Gene‑Therapy Deal Worth Up to $12.47 a Share

The offer targets Ixo-vec, a one-time treatment for wet age-related macular degeneration now in a late-stage trial.

FDA Names First 9 Drugs for ‘National Priority’ Fast-Track Reviews, Targeting 1–2-Month Decisions

AI-Guided Pythia Steers CRISPR Edits Toward Precise DNA Integration

Sarepta Defies FDA, Keeps Duchenne Gene Therapy on the Market

Early Temferon Trial Shows Engineered Macrophages Reprogram Glioblastoma Niche to Rescue CAR-T Cells

Scientists Uncover Genetic ‘Dimmer Switch’ That Tunes Embryonic Gene Expression

FDA Investigates Fatal Liver Failures Linked to Sarepta’s Elevidys Therapy

CRISPR Technique Reawakens Dormant Genes to Treat Blood Disorders

Sarepta Halts Elevidys Shipments for Non-Ambulatory Patients After Second Fatal Liver Failure

Study uncovers early-life window for in vivo gene therapy of blood stem cells