Health ❯ Genetics

Gene Therapy

Induced Pluripotent Stem Cells Hereditary Deafness CRISPR Technology Experimental Treatment Gaucher Disease GBA1 Gene Cell-Based Therapies Mucopolysaccharidosis Type II

5 ARTICLES

7mo ago

Ambroxol Trial Confirms Safety, Brain Delivery and Early Cognitive Benefits in Parkinson’s Dementia

Phase 2 results showing stable biomarkers with improved cognition in genetically at-risk patients pave the way for a larger cognition-focused study later this year.

7 ARTICLES

7mo ago

Ambroxol Demonstrates Safety and Neuroprotection Signals in Parkinson’s Dementia Trial