Gene Therapy

CRISPR Topical Gene Therapy Duchenne Muscular Dystrophy Sickle Cell Disease Treatment Gene-Editing Treatment Blood Disorders Gene-Editing Tools Bone Marrow Transplant Casgevy Treatment Sickle-Cell Disease Treatment Crispr Gene Editing CRISPR-based Medicine CRISPR/Cas9 Blood Diseases Crispr Casgevy Gene-Editing Therapy CRISPR Gene Editing CRISPR-Based Treatments Muscular Dystrophy Immunotherapy

26 ARTICLES

last yr.

UK Approves World's First CRISPR-Based Treatment for Blood Disorders

The groundbreaking gene-editing therapy, Casgevy, offers a potential cure for sickle cell disease and beta thalassemia, but concerns about accessibility and safety remain.

4 ARTICLES

last yr.

Gene therapy eyedrops restore boy's sight, offer hope for millions with eye diseases

12 ARTICLES

last yr.

FDA Approves $3.2 Million Gene Therapy for Fatal Childhood Disease Despite Research Concerns

3 ARTICLES

2y ago

Bluebird Bio Files for FDA Approval of Gene Therapy Treatment for Sickle Cell Disease