Science ❯Medical Research

Gene Therapy

Clinical Trials Treatment Innovations Fetal Hemoglobin Research Innovative Treatments Public Health Innovations Genetic Disorders CRISPR Technology

NHS Approves First Gene-Editing Therapy for Severe Sickle Cell Disease

The groundbreaking treatment, Casgevy, offers hope for a functional cure using Nobel Prize-winning Crispr technology.

Pfizer Withdraws Sickle Cell Drug Oxbryta Over Safety Concerns

Breakthrough Gene Therapies Offer New Hope for Sickle Cell Disease