Science ❯Biotechnology ❯Genetic Engineering

Therapeutic Applications

Animal Models Gene Therapy Safety Clinical Trials

Sarepta Defies FDA, Keeps Duchenne Gene Therapy on the Market

Regulators have placed limb-girdle muscular dystrophy trials on hold to assess Elevidys’s safety after three liver-failure deaths.

First Personalized CRISPR Therapy Saves Infant with Rare Metabolic Disorder