Science ❯ Genetics

Gene Therapy

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Aurora Therapeutics Launches to Scale Bespoke Gene Editing for PKU

Co-founded by Jennifer Doudna with Fyodor Urnov, the startup plans to use a base-editing platform under the FDA’s “plausible mechanism” pathway.

FDA Meeting Minutes Undercut uniQure’s Plan to File Huntington’s Gene Therapy for Approval

Regeneron, Tessera Strike $150 Million Gene-Editing Pact for Alpha‑1 Antitrypsin Deficiency

Lowering a Brain Protein Reverses Age-Related Memory Deficits in Mice

FDA Approves Zevaskyn Gene Therapy for Healing Large Epidermolysis Bullosa Wounds

FDA Halts Rocket’s RP-A501 Gene Therapy for Danon Disease After Patient’s Death