Science ❯Genetics

Gene Therapy

Protein Engineering Hearing Loss Otoferlin Gene Neuronal Plasticity Sickle Cell Disease LAMP2 Gene Follistatin Deafness Personalized Medicine Clinical Trials

FDA Approves Zevaskyn Gene Therapy for Healing Large Epidermolysis Bullosa Wounds

VIITAL study results demonstrate durable wound closure with prademagene zamikeracel in patients with recessive dystrophic EB

FDA Halts Rocket’s RP-A501 Gene Therapy for Danon Disease After Patient’s Death

Breakthrough Gene Therapies Offer New Hope for Sickle Cell Disease

Zebrafish Reveal New Pathways for Spinal Cord Injury Recovery

Gene Therapy Restores Hearing in Children with Hereditary Deafness