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Praxis Relutrigine Study Halted Early for Efficacy as FDA Review Meeting Set

The readout advances a potential first targeted therapy for severe SCN2A and SCN8A epilepsies.

Overview

  • An independent data monitoring committee recommended stopping the EMBOLD registrational cohort early based on efficacy.
  • The FDA confirmed a meeting in the coming weeks to review the EMBOLD data, after which Praxis will decide on NDA timing for relutrigine.
  • Praxis will present topline EMBOLD results on December 6 at the American Epilepsy Society Annual Meeting in Atlanta.
  • Praxis shares jumped roughly 25%–31% on Friday as HC Wainwright raised relutrigine’s probability of success to 80% and boosted its price target and peak sales estimates.
  • In a separate update, Praxis completed a pre‑NDA meeting for ulixacaltamide for essential tremor and expects to submit an NDA in early 2026.