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Neurocrine’s Valbenazine Misses Phase 3 Goals in Dyskinetic Cerebral Palsy

Full results will be detailed at a scientific meeting, with safety findings in line with the drug’s established profile.

Overview

  • The randomized, double-blind, placebo-controlled KINECT-DCP study ran 14 weeks and enrolled participants ages 6 to 70.
  • The trial’s primary endpoint assessing improvement in chorea was not met, and key secondary measures also failed.
  • Neurocrine said adverse events were generally consistent with prior experience for valbenazine.
  • The company noted there are no approved therapies for dystonia or choreoathetosis in cerebral palsy, and its CMO called the outcome disappointing.
  • Shares fell about 1% following the announcement, and at least one analyst forecast limited impact on the broader investment thesis.