Gene Therapy Shows Dramatic Vision Restoration in Rare Eye Condition
Patients with Leber congenital amaurosis experience significant improvements in vision following innovative treatment.
- Clinical trial participants saw up to a 10,000-fold increase in light sensitivity.
- The therapy, ATSN-101, was injected under the retina and tested in varying doses.
- Significant improvements in reading and navigation abilities were noted.
- Most side effects were minor and related to the surgical procedure.
- Further trials are planned to confirm safety and efficacy for broader use.