Particle.news
Download on the App Store

FDA Approves Breyanzi for Marginal Zone Lymphoma After Two or More Therapies

The decision rests on phase 2 data showing high response rates with labeling that highlights cytokine release syndrome and neurologic risks.

Overview

  • Breyanzi becomes the only CD19-directed CAR T-cell therapy cleared for marginal zone lymphoma and its fifth approved indication overall.
  • Approval is based on the TRANSCEND FL phase 2 cohort, where the intention-to-treat population had an 84.4% overall response rate and a 55.8% complete response rate, with median duration of response not reached.
  • Bristol Myers Squibb reported a 95.5% response rate with 62.1% complete responses in a third-line-or-later analysis set, reflecting a different efficacy denominator than the intention-to-treat summary.
  • Safety information cites cytokine release syndrome in 76% of patients, including 4.5% grade 3 or higher, with neurologic events such as headache and encephalopathy each seen in 21% of patients.
  • The one-time list price is about $567,237, and the company says the therapy is broadly covered by commercial and government insurers.