CRISPR Gene Therapy Shows Promising Results in Treating Inherited Blindness
A recent clinical trial demonstrates significant vision improvements in patients with Leber Congenital Amaurosis using CRISPR gene-editing technology.
- The trial involved 14 participants with measurable improvements reported in 79% of cases.
- CRISPR-based gene therapy was administered directly inside the body, marking a first in medical applications.
- No serious adverse events were reported, affirming the safety of the treatment in a clinical setting.
- Researchers emphasize the need for further studies to optimize dosing and expand patient demographics.
- The breakthrough offers potential for treating other inherited retinal diseases and genetic disorders.
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